CRISPR RNA Targeting Tool Comparison for UBE3A Unsilencing in Angelman Syndrome
Ulrika Beitnere, Tomas Salter-Cid, Miranda S. Garcia,Henriette O'Geen,David Colognori, Madison Drea Hypes, He E. Yang,Timothy A. Fenton, Harry M. Chen, Benjamin D. Brophy,Casiana E. Gonzalez, Paula A. Vij,Kyle D. Fink,Jill L. Silverman,Jennifer A. Doudna,David J. Segal MOLECULAR THERAPY(2023)
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