A Phase 2 Clinical Trial Evaluating the Safety and Efficacy of SRP-9001 for Treating Patients with Duchenne Muscular Dystrophy (S23.002)
Jerry R. Mendell,Perry B. Shieh,Zarife Sahenk,Kelly J. Lehman,Linda P. Lowes,Natalie F. Reash,Megan A. Iammarino,Lindsay N. Alfano,Brenna Powers,Jeremy D. Woods,Christy L. Skura,Howard C. Mao,Loretta A. Staudt,Rachael A. Potter,Danielle A. Griffin,Sarah Lewis,Larry Hu,Sameer Upadhyay,Teji Singh,Louise R. Rodino-Klapac Neurology(2022)
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