GO-8: Stable Expression of Factor VIII over 5 Years Following Adeno-Associated Gene Transfer in Subjects with Hemophilia a Using a Novel Human Factor VIII Variant

Pratima Chowdary,Ulrike M. Reiss,Edward G. D. Tuddenham,Paul Batty,Jenny H. McIntosh,Vlad Calin Radulescu, Eugenia Chang,Michael A. Laffan,Anne Riddell, Joanna C. M. Calvert, Arnulfo Pie, Rita Peralta, Upuli Pabakumari Dissanayake, Kirollos Kamel, Bharath Ram Sreedhar,Junfang Zhou,Guolian Kang, Yunus Olufadi,Michael M. Meagher,Christopher L. Morton, Alison J. Evans, Andrew M. Davidoff, Amit C. Nathwani

BLOOD(2023)

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