AAV-Mediated LINC Complex Uncoupling Ameliorates Pathology in a Mouse Model of LMNA Dilated Cardiomyopathy

Hendrikje Werner, Esther S. Gan, Connie Loh, Jennifer Ng,Nyein Thet Khaing,Jinqiu Zhang, Mervyn Ong, John Lee, David W. Russell, Yann Chong Tan,Colin Stewart,Brian Burke,Yin Loon Lee

CIRCULATION(2023)

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关键词
Cardiomyopathy,Gene therapy,Gene mutations
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