Psychometric validation of Pompe Disease Symptom Scale (PDSS) and Pompe Disease Impact Scale (PDIS) in patients with lateonset Pompe disease: A real-world evidence study

Ruth Pulikottil-Jacob, Neeraj Singh Rawat, Doug Altenweg,Chad Gwaltney,Laurence Pollissard

MOLECULAR GENETICS AND METABOLISM(2024)

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